At a glance
- What the study gets you
- Access to the study treatment being tested
- Type of study
- Interventional (receives a drug or procedure)
- Time in hospital
- In-person visits at study sites — visit count not specified by the sponsor
- Drug or intervention
- CTX310 (drug)
- How long the study runs
- Study runs about 48 months (dates as stated)
- About the drug or intervention
- CTX310 — drug: CTX310 is a lipid nanoparticle (LNP) formulation of clustered regularly interspaced short palindromic repeats (CRISPR)-associated protein 9 (Cas9) components for in vivo editing of the target gene angiopoietin-like 3 (ANGPTL3).
- Patient visit burden
- Not specified by the sponsor
- Type of study
- Testing a treatment
- Ages
- 18 Years to 75 Years
- Who
- All
- Number of participants
- 90
- Started
- 2024-06-21
- Last checked
- 2026-09
Plain English Summary
What is this study?
- • Testing a new treatment for cardiovascular
- • Phase1 - 90 participants
- • This is a single-arm, open-label, multicenter, ascending dose Phase 1 trial that will enroll participants 18 to 75 years of age with dyslipidemias that are refractory to available treatments
Who can take part?
- • Ages 18 Years to 75 Years
- • Diagnosed with cardiovascular
Where?
- • Cambridge - Royal Papworth Hospital
- • London - Richmond Pharmacology
This is a simplified summary. Always discuss with your doctor before making any decisions.
About This Trial
This is a single-arm, open-label, multicenter, ascending dose Phase 1 trial that will enroll participants 18 to 75 years of age with dyslipidemias that are refractory to available treatments.
More detail
This is a phase 1, open-label, multi-center study of CTX310 in participants with refractory dyslipidemias. Subjects will receive a dose of CTX310 via intravenous (IV) infusion.
How this trial compares with your answers
Answer 2 more questions to improve match
What we know so far
Still need:
- • Tell us your age for better matching
- • Tell us your sex for better matching
Preliminary match based on your answers. Full eligibility requires on-site assessment including medical history, physical exam, and lab tests. This does not guarantee enrolment.
Eligibility at a Glance
Key info
- Age: 18 Years - 75 Years
- Who can join: All genders
What the study is looking for
- ✓Age of ≥18 and ≤75 years at the time of signing the agreement to take part.
- ✓Able to provide written agreement to take part.
- ✓Refractory to the maximal intensity or MTD of the usual treatment lines of lipid-lowering therapies available through...
- ✓Female participants must be postmenopausal or surgically sterile.
- ✓All male participants and their female partners must agree to the use of an acceptable method of effective...
Who cannot take part
- ✗Participants with familial chylomicronemia syndrome (FCS). Some exceptions may apply.
- ✗Evidence of liver disease, defined as but not limited to:
- ✗LFTS \>2 × upper limit of normal (ULN), or total liver blood test \>2 × ULN, or INR \>1.5 × ULN, or liver stiffness...
- ✗Abnormal or compromised function of kidney, heart, blood or liver.
- ✗Acute coronary syndrome event or stroke within 24 weeks prior to Day 1. Acute pancreatitis within 12 weeks prior to...
See the full criteria
Where Is This Study? (2 UK sites)
Royal Papworth Hospital
Cambridge, United Kingdom
Richmond Pharmacology
London SE1 1YR, United Kingdom
How to Get in Touch
Clinical Trials
Sponsor contactCONTACT
